InterviewCelebrating Hope on Spinal Muscular Atrophy (SMA)
There were no treatment options available for the nearly 9,000 individuals in the United States living with a rare disease called spinal muscular atrophy (SMA) until December 2016.[1] Individuals with SMA often experienced symptoms related to the deteriorating effects of the condition, which may include the gradual onset of muscle weakness, which can lead to the inability to stand or walk independently [2]. To learn more about the topic, we conducted an interview with Dr....










